The $2.1 Million Answer: Why Dubai Is the Only Hope for the World’s Rarest Genetic Diseases
The Crisis Point: When Only Gene Therapy Will Save a Life For families dealing with an ultra-rare genetic condition like Spinal Muscular Atrophy (SMA) or certain metabolic disorders, the treatment is not a pill or a surgery; it is a $2.1 million, one-time gene therapy infusion. This is the financial frontier of medicine, and only … Read more